TAKING AIM
AT THE CAUSE OF
GENETIC DISEASE
Advancing science with curative potential for genetically mediated cardiovascular and neurological diseases
Our approach
Our strategy centers on high-impact genetic medicine candidates for cardiovascular and neurological diseases, prioritizing efficient development, advanced manufacturing, and strategic partnerships.
Our Team
Building on groundbreaking research from Weill Cornell Medicine and the University of California San Diego, we partner with preeminent institutions on the cutting edge of genetic disease research.
